Publications

Phase 1-2 Trial of Antisense Oligonucleotide Tofersen for SOD1 ALS

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Miller T, Cudkowicz M, Shaw P, Andersen P, Nazem A, Bucelli R, Genge A, Glass J, Ladha S, Ludolph A, Maragakis N, McDermott C, Pestronk A, Ravits J, Salachas F, Trudell R, Van Damme P, Zinman L, Bennett CF, Lane R, Sandrock A, Runz H, Graham D, Houshyar H, McCampbell A, Nestorov I, Chang I, McNeill M, Fanning L, Fradette S, Ferguson T.